[1] The most common side effects include abdominal pain, difficulty swallowing, upper respiratory tract infections, and vomiting.

[4] Levacetylleucine is indicated for the treatment of neurological manifestations of Niemann-Pick disease type C in people weighing at least 15 kilograms (33 lb).

[1][2] The most common side effects include abdominal pain, difficulty swallowing, upper respiratory tract infections, and vomiting.

[1][2] The safety and efficacy of levacetylleucine for the treatment of Niemann-Pick disease type C were evaluated in a randomized, double-blind, placebo-controlled, two-period, 24-week crossover study.

[2] To be eligible for the study participants had to be four years of age or older with a confirmed diagnosis of Niemann-Pick disease type C and at least mild disease-related neurological symptoms.