The n-Lorem Foundation is a non-profit organization based in Carlsbad, California, established to develop personalized medicines using antisense RNA in order to treat patients of rare diseases.
[3] The n-Lorem Foundation was established in January 2020 with the goal of taking advantage of the technology developed at Ionis to provide experimental treatments to patients suffering from rare genetic disorders.
Patients with extremely rare genetic disorders have numerous unique challenges to face when seeking treatment.
[4] The development of any drug for treating patients with nano-rare genetic disorders then, must be very efficient in time and price.
[6] To bring experimental antisense oligonucleotide (ASO) therapies to patients with extremely rare diseases for free, for life.