Marina Cavazzana is a professor of Paediatric Immunology at the Necker-Enfants Malades Hospital and the Imagine Institute, as well as an academic at Paris Descartes University.

[2] She established the first Clinical Investigation Center in the Assistance Publique – Hôpitaux de Paris, which is the only French academic department is authorised to produce cell and gene therapies.

[5] Cavazzana was the first doctor to successfully treat a boy with sickle cell disease, a severe form of hereditary chronic anemia.

The first gene therapy trail of young boys with X-linked severe combined immunodeficiency was performed by Cavazzana in collaboration with bluebird bio in 2000.

[11] The law requires close family members to be informed when individuals are at risk of developing a genetically transmitted illness.